The POLG Foundation — Biomedical Watch V2

Traitements2programmes

Essais1liés

Publications0liées

SourceDBlocale

Traitements

2

Molécule	Indication / population	Phase	Objectif	Pays	Résultat
PIONEER — Prospective Natural History Study of POLG DiseaseThe PIONEER study is a prospective, natural history study dedicated to characterizing the clinical progression of POLG-related disorders. The research aims to bridge the gap between genetic diagnosis and drug development by mapping how these rare mitochondrial conditions evolve over time. By observing the disease's natural trajectory through a multi-center approach, The study identifies critical clinical milestones that serve as a foundation for evaluating therapeutic efficacy and future therapeutic interventions	Épilepsie	À vérifier	Remyélinisation indirecte / réparation + Ralentissement de la progression	United States	À vérifier
PIONEER — Prospective Natural History Study of POLG DiseaseThe PIONEER study is a prospective, natural history study dedicated to characterizing the clinical progression of POLG-related disorders. The research aims to bridge the gap between genetic diagnosis and drug development by mapping how these rare mitochondrial conditions evolve over time. By observing the disease's natural trajectory through a multi-center approach, The study identifies critical clinical milestones that serve as a foundation for evaluating therapeutic efficacy and future therapeutic interventions	Épilepsie	À vérifier	Remyélinisation indirecte / réparation + Ralentissement de la progression	United States	À vérifier

Essais cliniques

1

Molécule	Indication / population	Phase	NCT	Titre	Statut
PIONEER — Prospective Natural History Study of POLG Disease	Épilepsie	À vérifier	NCT07775872	PIONEER — Prospective Natural History Study of POLG Disease	NOT_YET_RECRUITING

Publications

0

Molécule	Indication / population	Titre	Journal	Date
Aucune publication.